Open-label evaluation of oral trehalose in patients with neuronal ceroid lipofuscinoses

Stefania Della Vecchia, Nicola Gammaldi, Ivana Ricca, Serena Mero, Stefano Doccini, Anna Ardissone, Silvia Bagnoli, Roberta Battini, Elisa Colombi, Jacopo Favaro, Roberto Furlan, Lucio Giordano, Assunta Ingannato, Alessandra Mandelli, Francesca Maria Paola Manzoni, Giuseppe Milito, Isabella Moroni, Benedetta Nacmias, Nardo Nardocci, Lucio ParmeggianiFrancesco Pezzini, Nicola Pietrafusa, Stefano Sartori, Nicola Specchio, Marina Trivisano, Alessandro Simonati, Filippo Maria Santorelli, A-NCL ETS Group

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Immunology and Microbiology