Improved Double-Nicking Strategies for COL7A1-Editing by Homologous Recombination.

Thomas Kocher (First author), Roland N Wagner, Alfred Klausegger (Co-author), Christina Guttmann-Gruber (Co-author), Stefan Hainzl (Co-author), Johann Bauer (Co-author), Julia Reichelt (Co-author), Ulrich Koller* (Last author)

*Corresponding author for this work

Research output: Contribution to journalOriginal Articlepeer-review

34 Citations (Web of Science)
Original languageEnglish
Pages (from-to)496-507
JournalMolecular Therapy - Nucleic Acids
Volume18
DOIs
Publication statusPublished - 2019

Keywords

  • FIBROBLAST CELL THERAPY
  • EPIDERMOLYSIS-BULLOSA
  • STEM-CELLS
  • WEB TOOL
  • COL7A1
  • CRISPR/CAS9
  • CAS9
  • MUTATION
  • COLLAGEN
  • REPAIR

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