Highly efficient paired nickase-mediated correction of junctional epidermolysis bullosa via COL17A1 reframing

Oliver March, Thomas Kocher, Bernadette Liemberger, Johannes Bischof, Stefan Hainzl, S Haas, Anna Hochreiter, Dirk Strunk, T Cathomen, Julia Reichelt, Johann Bauer, Ulrich Koller

Research output: Contribution to journalAbstract (Journal)peer-review

Original languageEnglish
Pages (from-to)A173-A173
JournalHUMAN GENE THERAPY
Volume30
Issue number11
Publication statusPublished - 2019
EventESGCT 27th Annual Congress in collaboration with SETGyc Meeting - Barcelona, SPAIN
Duration: 22 Oct 201925 Oct 2019

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