Early access experience with VPRIV(®): recommendations for "core data" collection.

Derralynn A Hughes; Moeen Al-Sayed; Nadia Belmatoug; Olaf A. Bodamer; Tobias Böttcher; Maria Cappellini; Ian J Cohen; Terence Eagleton; Deborah Elstein; Pilar Giraldo; Simon Jones; Chaim Kaplinsky; Allan Lund; Maciej Machaczka; Eugen Mengel; Gregory M Pastores; Hanna Rosenbaum; Malvin Sjo; Nikolaus Tiling; Panagiotis Tsaftaridis; Ari Zimran; Neal Weinreb

doi:10.1016/j.bcmd.2010.10.015

Early access experience with VPRIV(®): recommendations for "core data" collection.

Derralynn A Hughes, Moeen Al-Sayed, Nadia Belmatoug, Olaf A. Bodamer (Co-author), Tobias Böttcher, Maria Cappellini, Ian J Cohen, Terence Eagleton, Deborah Elstein, Pilar Giraldo, Simon Jones, Chaim Kaplinsky, Allan Lund, Maciej Machaczka, Eugen Mengel, Gregory M Pastores, Hanna Rosenbaum, Malvin Sjo, Nikolaus Tiling, Panagiotis TsaftaridisAri Zimran, Neal Weinreb

Department of Pediatrics

Research output: Contribution to journal › Letter to the editor › peer-review

3 Citations (Web of Science)

Original language	English
Pages (from-to)	140-142
Journal	BLOOD CELLS MOLECULES AND DISEASES
Volume	47
Issue number	2
DOIs	https://doi.org/10.1016/j.bcmd.2010.10.015
Publication status	Published - 2011

Keywords

ENZYME REPLACEMENT THERAPY
TYPE-1 GAUCHER-DISEASE
VELAGLUCERASE ALPHA

Access to Document

10.1016/j.bcmd.2010.10.015

Cite this

Hughes, D. A., Al-Sayed, M., Belmatoug, N., Bodamer, O. A., Böttcher, T., Cappellini, M., Cohen, I. J., Eagleton, T., Elstein, D., Giraldo, P., Jones, S., Kaplinsky, C., Lund, A., Machaczka, M., Mengel, E., Pastores, G. M., Rosenbaum, H., Sjo, M., Tiling, N., ... Weinreb, N. (2011). Early access experience with VPRIV(®): recommendations for "core data" collection. BLOOD CELLS MOLECULES AND DISEASES , 47(2), 140-142. https://doi.org/10.1016/j.bcmd.2010.10.015

Hughes, Derralynn A ; Al-Sayed, Moeen ; Belmatoug, Nadia et al. / Early access experience with VPRIV(®): recommendations for "core data" collection. In: BLOOD CELLS MOLECULES AND DISEASES 2011 ; Vol. 47, No. 2. pp. 140-142.

@article{004c7ce3e66e4872acf0c9d79543a8eb,

title = "Early access experience with VPRIV({\textregistered}): recommendations for {"}core data{"} collection.",

keywords = "ENZYME REPLACEMENT THERAPY, TYPE-1 GAUCHER-DISEASE, VELAGLUCERASE ALPHA",

author = "Hughes, \{Derralynn A\} and Moeen Al-Sayed and Nadia Belmatoug and Bodamer, \{Olaf A.\} and Tobias B{\"o}ttcher and Maria Cappellini and Cohen, \{Ian J\} and Terence Eagleton and Deborah Elstein and Pilar Giraldo and Simon Jones and Chaim Kaplinsky and Allan Lund and Maciej Machaczka and Eugen Mengel and Pastores, \{Gregory M\} and Hanna Rosenbaum and Malvin Sjo and Nikolaus Tiling and Panagiotis Tsaftaridis and Ari Zimran and Neal Weinreb",

note = "University Children's Hospital Salzburg, Salzburg, Austria",

year = "2011",

doi = "10.1016/j.bcmd.2010.10.015",

language = "English",

volume = "47",

pages = "140--142",

journal = "BLOOD CELLS MOLECULES AND DISEASES ",

issn = "1079-9796",

number = "2",

}

Hughes, DA, Al-Sayed, M, Belmatoug, N, Bodamer, OA, Böttcher, T, Cappellini, M, Cohen, IJ, Eagleton, T, Elstein, D, Giraldo, P, Jones, S, Kaplinsky, C, Lund, A, Machaczka, M, Mengel, E, Pastores, GM, Rosenbaum, H, Sjo, M, Tiling, N, Tsaftaridis, P, Zimran, A & Weinreb, N 2011, 'Early access experience with VPRIV(®): recommendations for "core data" collection.', BLOOD CELLS MOLECULES AND DISEASES , vol. 47, no. 2, pp. 140-142. https://doi.org/10.1016/j.bcmd.2010.10.015

Early access experience with VPRIV(®): recommendations for "core data" collection. / Hughes, Derralynn A; Al-Sayed, Moeen; Belmatoug, Nadia et al.
In: BLOOD CELLS MOLECULES AND DISEASES , Vol. 47, No. 2, 2011, p. 140-142.

Research output: Contribution to journal › Letter to the editor › peer-review

TY - JOUR

T1 - Early access experience with VPRIV(®): recommendations for "core data" collection.

AU - Hughes, Derralynn A

AU - Al-Sayed, Moeen

AU - Belmatoug, Nadia

AU - Bodamer, Olaf A.

AU - Böttcher, Tobias

AU - Cappellini, Maria

AU - Cohen, Ian J

AU - Eagleton, Terence

AU - Elstein, Deborah

AU - Giraldo, Pilar

AU - Jones, Simon

AU - Kaplinsky, Chaim

AU - Lund, Allan

AU - Machaczka, Maciej

AU - Mengel, Eugen

AU - Pastores, Gregory M

AU - Rosenbaum, Hanna

AU - Sjo, Malvin

AU - Tiling, Nikolaus

AU - Tsaftaridis, Panagiotis

AU - Zimran, Ari

AU - Weinreb, Neal

N1 - University Children's Hospital Salzburg, Salzburg, Austria

PY - 2011

Y1 - 2011

KW - ENZYME REPLACEMENT THERAPY

KW - TYPE-1 GAUCHER-DISEASE

KW - VELAGLUCERASE ALPHA

U2 - 10.1016/j.bcmd.2010.10.015

DO - 10.1016/j.bcmd.2010.10.015

M3 - Letter to the editor

C2 - 21146428

SN - 1079-9796

VL - 47

SP - 140

EP - 142

JO - BLOOD CELLS MOLECULES AND DISEASES

JF - BLOOD CELLS MOLECULES AND DISEASES

IS - 2

ER -

Hughes DA, Al-Sayed M, Belmatoug N, Bodamer OA, Böttcher T, Cappellini M et al. Early access experience with VPRIV(®): recommendations for "core data" collection. BLOOD CELLS MOLECULES AND DISEASES . 2011;47(2):140-142. doi: 10.1016/j.bcmd.2010.10.015