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Context-Dependent Strategies for Enhanced Genome Editing of Genodermatoses.

Research output: Contribution to journal › Review article › peer-review

30 Citations (Web of Science)
Original languageEnglish
JournalCELLS
Volume9
Issue number1
DOIs
Publication statusPublished - 2020

Keywords

  • TERMINATION CODON MUTATION
  • PLURIPOTENT STEM-CELLS
  • EPIDERMOLYSIS-BULLOSA
  • DNA-REPAIR
  • MUSCULAR-DYSTROPHY
  • GENE CORRECTION
  • COL7A1 MUTATION
  • CRISPR/CAS9
  • BASE
  • EXON

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