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Considerations for a Successful RNA Trans-splicing Repair of Genetic Disorders.

Research output: Contribution to journalOriginal Articlepeer-review

23 Citations (Web of Science)
Original languageEnglish
Pages (from-to)e157
JournalMolecular Therapy - Nucleic Acids
Volume3
DOIs
Publication statusPublished - 2014

Keywords

  • MESSENGER-RNA
  • REPLACEMENT
  • MOLECULES
  • PROTEIN
  • SYSTEM

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