An ex vivo RNA trans-splicing strategy to correct human generalized severe epidermolysis bullosa simplex.

Patricia Peking (First author), Jenny Breitenbach (First author), Michael Ablinger (Co-author), Wolfgang Muss, F J Poetschke, Thomas Kocher (Co-author), Ulrich Koller (Co-author), Stefan Hainzl (Co-author), S Kitzmueller, Johann Bauer (Co-author), Julia Reichelt (Co-author), Thomas Lettner (Last author), Verena Wally* (Last author)

*Corresponding author for this work

Research output: Contribution to journalOriginal Article (Journal)peer-review

23 Citations (Web of Science)
Original languageEnglish
Pages (from-to)141-148
JournalBRITISH JOURNAL OF DERMATOLOGY
Volume180
Issue number1
DOIs
Publication statusPublished - 2019

Keywords

  • GENE-THERAPY
  • MOUSE MODEL
  • REPAIR
  • COL7A1
  • TRANSPLANTATION
  • KERATINOCYTES
  • IMPROVEMENT
  • DEFICIENCY
  • DIACEREIN
  • CELLS

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