Advances in gene editing strategies for epidermolysis bullosa.

Thomas Kocher (First author), Ulrich Koller* (Last author)

*Corresponding author for this work

Research output: Contribution to journalOriginal Articlepeer-review

8 Citations (Web of Science)
Original languageEnglish
Pages (from-to)8-109
JournalPROGRESS IN MOLECULAR BIOLOGY AND TRANSLATIONAL SCIENCE
Volume182
DOIs
Publication statusPublished - 2021

Keywords

  • KERATIN INTERMEDIATE-FILAMENTS
  • TERMINATION CODON MUTATION
  • STEM-CELLS
  • RETROVIRAL VECTORS
  • COL7A1 MUTATION
  • CRISPR CAS9
  • GENOMIC DNA
  • SIMPLEX
  • THERAPY
  • REPAIR

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