A novel screening system improves genetic correction by internal exon replacement.

Research output: Contribution to journalOriginal Articlepeer-review

27 Citations (Web of Science)
Original languageEnglish
Pages (from-to)e108
JournalNUCLEIC ACIDS RESEARCH
Volume39
Issue number16
DOIs
Publication statusPublished - 2011

Keywords

  • EPIDERMOLYSIS-BULLOSA
  • REPAIR
  • THERAPY
  • PROSPECTS

Cite this