State-of-the-art statistical design and analysis for maximal success with minimal patient burden in Epidermolysis bullosa trials

Project: Research

A neutral comparison of statistical methods for analyzing longitudinally measured ordinal outcomes in rare diseases.
Geroldinger, M. (First author), Verbeeck, J., Thiel, K. E. (Co-author), Molenberghs, G., Bathke, A. C., Laimer, M. (Co-author) & Zimmermann, G. J. (Last author), 2023, In: BIOMETRICAL JOURNAL. BIOMETRISCHE ZEITSCHRIFT. p. e2200236
Research output: Contribution to journal › Original Article › peer-review

5 Citations (Web of Science)
How to analyze continuous and discrete repeated measures in small-sample cross-over trials?
Verbeeck, J., Geroldinger, M. (Co-author), Thiel, K. (Co-author), Hooker, A., Ueckert, S., Karlsson, M., Bathke, A., Bauer, J. (Co-author), Molenberghs, G. & Zimmermann, G. J. (Last author), 2023, In: BIOMETRICS.
Research output: Contribution to journal › Original Article › peer-review

5 Citations (Web of Science)
Statistical recommendations for count, binary, and ordinal data in rare disease cross-over trials
Geroldinger, M. (First author), Verbeeck, J., Hooker, A. C., Thiel, K. E. (Co-author), Molenberghs, G., Nyberg, J., Bauer, J. (Co-author), Laimer, M. (Co-author), Wally, V. (Co-author), Bathke, A. C. & Zimmermann, G. (Last author), 19 Dec 2023, In: ORPHANET JOURNAL OF RARE DISEASES. 18, 1, p. 391 12 p.
Research output: Contribution to journal › Original Article › peer-review

Open Access
2 Citations (Web of Science)

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