Project Details
| Status | Finished |
|---|---|
| Effective start/end date | 1/03/15 → 1/03/18 |
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An ex vivo RNA trans-splicing strategy to correct human generalized severe epidermolysis bullosa simplex.
Peking, P. (First author), Breitenbach, J. (First author), Ablinger, M. (Co-author), Muss, W., Poetschke, F. J., Kocher, T. (Co-author), Koller, U. (Co-author), Hainzl, S. (Co-author), Kitzmueller, S., Bauer, J. (Co-author), Reichelt, J. (Co-author), Lettner, T. (Last author) & Wally, V. (Last author), 2019, In: BRITISH JOURNAL OF DERMATOLOGY. 180, 1, p. 141-148Research output: Contribution to journal › Original Article › peer-review
25 Citations (Web of Science) -
Antisense RNA-mediated improvement of SMaRT therapy for KRT14 correction.
Liemberger, B., Lackner, N., Arzt, C., Hainzl, S., Wally, V., Kocher, T., Pinon Hofbauer, J., Murauer, E., Bauer, J., Reichelt, J. & Koller, U., 2018.Research output: Contribution to conference › Abstract
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RNA Trans-Splicing Modulation via Antisense Molecule Interference.
Liemberger, B. (First author), Piñón Hofbauer, J. (Co-author), Wally, V. (Co-author), Arzt, C. (Co-author), Hainzl, S. (Co-author), Kocher, T. (Co-author), Murauer, E. M. (Co-author), Bauer, J. (Co-author), Reichelt, J. (Co-author) & Koller, U. (Last author), 2018, In: INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES. 19, 3Research output: Contribution to journal › Original Article › peer-review
16 Citations (Web of Science)