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A three step approach to strong evidence on the impact of Enzyme-Replacement Therapy administered as Home Therapy in Gaucher, Fabry and Hunters disease

Project: Research

Project Details

StatusFinished
Effective start/end date15/05/1715/05/19

Collaborative partners

  • Dr. Vassiliki Konstantopoulou, Children Hospital, AKH, Vienna Medical University (lead)
  • Nicole Ettl, DKGS, Health Care at Home, Country Manager
  • Prof. Dr. Gere Sunder-Plassmann, Vienna Medical University
  • Dr. med. Jörg Reinke, Center for Paediatrics and Adolescent Medicine, Medical University Mainz, Germany
  • Michaela Weigl, MPS Austria
  • PD Dr. Esther Maier, Dr. v. Haunersches Kinderspital, Ludiwig-Maximilians University Munich, Germany
  • Franz Unterberger, DKGP, Healthcare at Home, Regional Manager